Memory failures often feel like personal lapses, but new research suggests the problem may be rooted in hidden architecture ...

With a new study in the journal Cell, researchers at Stanford University and Stockholm University have contributed to increased knowledge about gene regulation in human cells.

Encoded Therapeutics has linked its Dravet syndrome gene therapy ETX101 to a 78% reduction in seizures, keeping the biotech ...

Molecular and morphological profiles of developing neurons in vitro uncover the cellular dynamics of human neurodevelopment and related disease.

To continue reading this content, please enable JavaScript in your browser settings and refresh this page. Preview this article 1 min The FDA has restricted the type ...

Kyushu University researchers have created a novel “ACTG” naming system for human gene types, and launched the Joint Open ...

The FDA has officially limited the label of Sarepta Therapeutics’ Elevidys, putting an end to a whirlwind few months that saw the abrupt departure—and reinstatement—of top agency official Vinay Prasad ...

To continue reading this content, please enable JavaScript in your browser settings and refresh this page. Preview this article 1 min The FDA has restricted the ...

CAMBRIDGE, Mass. - Sarepta Therapeutics, Inc. (NASDAQ:SRPT) announced Friday that the prescribing information for ELEVIDYS, its gene therapy for Duchenne muscular dystrophy (DMD), has been updated ...

This valuable study provides solid evidence for deficits in aversive taste learning and taste coding in a mouse model of autism spectrum disorders. Specifically, the authors found that Shank3 knockout ...

The FDA has updated the labeling for Elevidys, a gene therapy for Duchenne muscular dystrophy (DMD), by adding its highest-level safety warning—a Boxed Warning—and restricting its approved use.